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Gene Editing in Hematologic Stem Cell Therapies

Gene Editing Techniques in Hematologic Stem Cell Therapy

Welcome to our article on gene editing techniques in hematologic stem cell therapy. Gene therapy holds immense promise in the field of medicine, offering the potential to treat various blood disorders by modifying the cell genome. In the context of hematologic stem cell therapy, gene editing techniques using programmable nucleases have shown remarkable advancements, bringing […]

CRISPR Therapeutics’ FDA Approval for CASGEVY™

FDA Approved sign

CRISPR Therapeutics has achieved a significant milestone with the U.S. Food and Drug Administration (FDA) approving CASGEVY™ (exagamglogene autotemcel [exa-cel]), a groundbreaking CRISPR/Cas9 gene-edited cell therapy. This approval makes CASGEVY available for the treatment of transfusion-dependent beta thalassemia (TDT) in patients aged 12 and older. Approximately 1,000 patients in the U.S. are now eligible for […]

RoslinCT and Lykan Bioscience Combine to Create Leading Advanced Cell Therapy CDMO

RoslinCT and Lykan logos

EDINBURGH, UK AND HOPKINTON, MA, 4 August 2022 – RoslinCT, a cell and gene therapy Contract Development and Manufacturing Organisation (‘CDMO’) developing life-changing therapies in Edinburgh’s BioQuarter, and Lykan Bioscience (‘Lykan’), an innovative CDMO focused on cell-based therapies, today announce that they have entered into a business combination agreement to form a global leading innovative […]

What is the Difference Between Gene Therapy, Cell Therapy, and Gene Editing?

Gene Therapy - DNA chain model

Gene therapy, cell therapy and gene editing are fields of biomedical research with similar goals in mind: To treat disease by changing our bodies at a microscopic level. Specifically, these approaches aim to change our genetic makeup. However, each one changes our genetic material in slightly different ways. What do these approaches have in common, […]